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Type
Biomedical and Pharmaceutical Research on the Development, Diagnosis, Prevention, and Treatment of Diseases
Shi, Q, Wilcox, DA, Fahs, SA, Weiler, H, Well, CC, Cooley, BC, Desai, D, Morateck, PA, Gorski, J, and Montgomery, RR. Factor VIII ectopically targeted to platelets is therapeutic in hemophilia A with high-titer inhibitory antibodies. J Clin Invest2006, 116 (7):1974-1982.10.1172/JCI28416CrossRefGoogle ScholarPubMed
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Shi, Q, Fahs, SA, Wilcox, DA, Kuether, EL, Morateck, PA, Mareno, N, Weiler, H, and Montgomery, RR. Syngeneic transplantation of hematopoietic stem cells (HSC) that are genetically modified to express factor VIII (FVIII) in platelets restores hemostasis to hemophilia A mice with pre-existing FVIII immunity. Blood2008,112 (7):2713-2721.10.1182/blood-2008-02-138214CrossRefGoogle Scholar
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